For the first time in Denmark, people with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene ...

Columnist Jennifer Lynne, a veteran of Florida hurricanes, offers advice for those with bleeding disorders should evacuations be necessary.

Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...

Columnist Joe MacDonald reflects on how the Parents Empowering Parents program helped him and his wife manage their son's hemophilia.

Columnist G Shellye Horowitz explains why she joined a federal lawsuit against a California law requiring licensing for out-of-state doctors.

Columnist Alliah Czarielle shares how video games helped her husband cope with hemophilia bleeds in the hospital when he was a child.

Be Biopharma has raised $92 million in series C financing to support the first-in-human Phase 1/2 trial of BE-101, the company’s B-cell therapy candidate for hemophilia B. “We are on track to ...

I don’t recall when I met Debbie Murray, but I remember the impression she left on me. Her frustration with the long and challenging journey to a proper diagnosis and effective treatment of her ...