The drug Elamipretide from Stealth BioTherapeutics treats an ultrarare, fatal disease called Barth syndrome. Small studies say it's safe and effective. But the FDA denied approval, leaving children ...

Argenx had cash, cash equivalents, and other short-term investments totaling $3.4 billion as of the end of 2024, making it well-positioned to continue funding its pipeline and commercialization ...

Novo Nordisk announced Monday that U.S. patients can now get a month's supply of Ozempic, the blockbuster diabetes drug, for $499, for those who pay for medications on their own and don't go through ...