Families of kids with PDCD are urging the FDA to approve DCA, a treatment that could extend their children's lives despite ...

September is National Sickle Cell Awareness Month in the USA, designated by Congress to help focus attention on the need for ...

A staggering 1 in 8 women in the United States will be diagnosed with breast cancer in their lifetime. In 2025 alone, an ...

Dementia is responsible for almost one in 10 of all deaths in Australia. Here are 5 expert-led ways to help future-proof your ...

The commercial success of existing lipid-lowering medications highlights the enormous market potential for effective cardiovascular therapies. Read more here.

RALEIGH, N.C. (WNCN) – Parents of children with ultra-rare diseases are encouraging the Food and Drug Administration to act quickly to approve drugs that could treat their conditions and to take into ...

Kerala has reported 72 infection and 19 deaths caused by brain-eating amoeba as compared to last year when 36 infections were reported, of which nine were fatal ...

President Donald Trump announced Monday that his administration is strongly recommending that women limit Tylenol use during ...

Was reportedly named after Keir Hardie, the first Labour leader in parliament. Starmer’s mother was diagnosed at a young age with Still’s disease, a rare inflammatory disorder that eventually left her ...

Can you have a heart attack and not know it? Silent heart attacks can be particularly dangerous because they often go unnoticed, and the damage may only be discovered later. In an interview with HT ...

The FDA’s proposed Rare Disease Evidence Principles review process is a starting point for getting rare disease therapies ...