Two Philadelphia doctors who led the groundbreaking gene-editing treatment of baby boy from Delaware County are included ...

Ultragenyx (NASDAQ:RARE) is one of the 10 Overlooked Growth Stocks to Buy Now.

Scientists discover salamander genes that help regrow limbs, using gene therapy to restore digit growth in mice.

For the roughly 80 million people worldwide living with glaucoma, daily life often means watching the world slowly close in.

A research team led by geneticist Jeannie Lee at Harvard Medical School, cell biologist Jeanne Lawrence at UMass Chan Medical ...

Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...

Three life-science prizes were awarded for advances in gene therapies. Opthalmologists Jean Bennett and Albert Maguire, and ...

The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell ...

Luxturna was the first FDA-approved gene therapy for a disease caused by mutations in a specific gene. It helped establish ...

Researchers have developed a modified CRISPR gene-editing tool with potential to silence the extra chromosome causing Down ...

From billionaire-backed biotech to promising animal studies, this early trial will test whether partial reprogramming can ...

Detroit patients getting HEMGENIX report life‑changing results; trial data show 94% off prophylaxis at five years.