Vertex Pharmaceuticals (NASDAQ: VRTX) and Mirum Pharmaceuticals (NASDAQ: MIRM) are two biotech stocks that share the same ...

Inside the deadly disease confounding medicine, researchers piecing together clues and the breakthrough that meant survival ...

The text messages motivate Christian Collins to keep inspiring others. One told the USC-bound forward about three family ...

A tiny antibody component could fundamentally transform the treatment of cystic fibrosis: For the first time, researchers ...

A tiny antibody component could fundamentally transform the treatment of cystic fibrosis: For the first time, researchers ...

Scientists now recognize that spontaneous DNA errors, which we acquire in early development all the way until our last breath ...

Knowing she could pass on a rare genetic condition called MEN-1 made the decision to have children feel impossibly heavy for ...

With a market cap of $112.9 billion, Vertex Pharmaceuticals Incorporated (VRTX) is a biotechnology company focused on ...

In a bar, a poet meets the man behind the drug that saved his life — discovering how science, faith and chance created a ...

About Sionna Therapeutics Sionna Therapeutics is a clinical-stage biopharmaceutical company on a mission to revolutionize the current treatment paradigm for cystic fibrosis (CF) by developing novel ...

India, April 5 -- Scientists caution that choosing embryos based on genetic scores raises urgent ethical risks and requires ...

The FDA has expanded indications for two targeted combination treatments, Alyftrek and Trikafta, that will now benefit more individuals with cystic fibrosis, according to a press release from the ...