Now, the work has been awarded the prestigious Breakthrough Prize at the "Oscars of Science." Today, Jean Bennett, MD, PHD, and Albert Maguire, MD, both emeritus professors of Ophthalmology in the ...

Luxturna was the first FDA-approved gene therapy for a disease caused by mutations in a specific gene. It helped establish ...

A lab in Hawaiʻi is developing nanobodies, tiny proteins that help the immune system recognize and destroy cancer cells, ...

Mayo Clinic scientists are exploring an unusual but promising strategy to treat one of the deadliest bile duct cancers by turning milk into a microscopic delivery system for gene therapy. Their work ...

The global gene therapy market size is projected to expand significantly, with an estimated value of USD 19.3 billion by 2034 ...

Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...

Since 2017, a personalized immunotherapy called Chimeric Antigen Receptor, or CAR-T cell treatment, has worked wonders to ...

Detroit patients getting HEMGENIX report life‑changing results; trial data show 94% off prophylaxis at five years.

Cancer drugs are designed to shut tumors down. But sometimes, in the very act of attacking a tumor, treatment can also help a ...

A new glioblastoma treatment showed tumour elimination and durable protection in a preclinical model. Discover what this ...

New experimental medications seem to extend survival with the hard-to-treat cancer.