Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a ...
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
Two Philadelphia doctors who led the groundbreaking gene-editing treatment of baby boy from Delaware County are included ...
J&J will hand over the rights to bota-vec for $25 million upfront, clearing MeiraGTx to seek regulatory approvals in the U.S.
The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell ...
Morning Overview on MSN
First human trial tests gene therapy aimed at reversing cellular aging
For the roughly 80 million people worldwide living with glaucoma, daily life often means watching the world slowly close in.
Pfizer announced in February 2025 that it was taking Beqvez (fidanacogene elaparvovec), its gene therapy for hemophilia B, ...
Roche is launching a new global phase 3 trial for the controversial Duchenne muscular dystrophy gene therapy Elevidys in ...
The FDA’s recently unveiled plausible mechanism framework may have been forged with i | The FDA’s newly launched plausible ...
Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.
Detroit patients getting HEMGENIX report life‑changing results; trial data show 94% off prophylaxis at five years.
Scientists discover salamander genes that help regrow limbs, using gene therapy to restore digit growth in mice.
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