Two Philadelphia doctors who led the groundbreaking gene-editing treatment of baby boy from Delaware County are included ...

The global gene therapy market size is projected to expand significantly, with an estimated value of USD 19.3 billion by 2034 ...

The ACC has published a scientific statement regarding the use of gene editing therapy for cardiovascular disease.

A compact Cas12f nuclease shows high editing efficiency in human cells, with structural insights enabling an engineered variant potentially suited for future AAV‑compatible delivery.

Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...

A research team led by geneticist Jeannie Lee at Harvard Medical School, cell biologist Jeanne Lawrence at UMass Chan Medical ...

New gene-editing techniques exploit unique chemical fingerprints in cancer DNA to selectively destroy tumor cells, paving the ...

Sensorineural hearing loss (SNHL) remains a global health challenge with limited regenerative therapeutic options. This ...

Researchers from The University of Texas MD Anderson Cancer Center will present initial data from six clinical trials during minisymposia at this week’s American Association for Cancer Research (AACR) ...

SAN DIEGO, APRIL 15, 2026 ― Researchers from The University of Texas MD Anderson Cancer Center will present initial data from six clinical trials ...