Inside the deadly disease confounding medicine, researchers piecing together clues and the breakthrough that meant survival ...

Vertex Pharmaceuticals on Monday reported disappointing first-quarter earnings impacted by weaker-than-expected sales of its drugs for cystic fibrosis, and little or no contributions from a gene ...

Genetic testing plays an important role in cystic fibrosis screening and diagnosis. It can help determine if a person has cystic fibrosis or carries gene mutations that cause it. Other tests can also ...

Vertex Pharmaceuticals, known for its line of cystic fibrosis drugs, has entered the gene editing space with a new $105 million deal with CRISPR Therapeutics. Cystic fibrosis has become the poster ...

States screen for cystic fibrosis (CF) but with significant variation among their screening algorithms. The Cystic Fibrosis Foundation group conducted a systematic review, leading to seven ...

Cystic fibrosis (CF) is a rare autosomal recessive disorder that affects numerous systems of the body. It is a complicated disease that differs from person to person. An autosomal recessive disorder ...

Managing expectations about the future and enjoying the responsibility and fulfilment of being a parent is now to the ...

Alyftrek (vanzacaftor/tezacaftor/deutivacaftor) is a combination medicine approved by the FDA in 2024. Alyftrek is approved to treat people ages 6 and older who have ...

Vertex Pharmaceuticals (NASDAQ: VRTX) and Mirum Pharmaceuticals (NASDAQ: MIRM) are two biotech stocks that share the same ...

Cystic fibrosis is a progressive, genetic disease that impacts organs including the lungs and pancreas. Almost 40,000 children and adults in the U.S. live with the disease, but thanks to advancements ...

Father-of-one Evan Wilson missed out of his son’s first Christmas and will likely miss out on his first birthday as well.

Regan Sparks, who has cystic fibrosis, takes medication that means she is not eligible for a visa. Regan Sparks tells the BBC why the Australian government won't grant her a Working Holiday Visa.