Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...

The FDA updated prescribing information for Elevidys with new safety warnings and limiting its use to DMD patients who can ...

New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...

With three sons with Duchenne MD, columnist Betty Vertin has little time for housework, making her regret not giving the other kids chores.

Columnist Shalom Lim reflects with gratitude on how he's found purpose by supporting other Singaporeans on their own health ...

Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.

A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.

What is Elevidys for Duchenne muscular dystrophy? Elevidys (delandistrogene moxeparvovec-rokl), previously known as SRP-9001, is a one-time gene therapy approved in the U.S. to treat patients with ...

A Phase 1/2 clinical trial testing SRP-1003, a treatment for myotonic dystrophy type 1 (DM1), is progressing as planned and continues to enroll patients at higher doses. The Phase 1/2 study ...