Two Philadelphia doctors who led the groundbreaking gene-editing treatment of baby boy from Delaware County are included ...
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
Luxturna was the first FDA-approved gene therapy for a disease caused by mutations in a specific gene. It helped establish ...
J&J will hand over the rights to bota-vec for $25 million upfront, clearing MeiraGTx to seek regulatory approvals in the U.S.
The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell ...
Pfizer announced in February 2025 that it was taking Beqvez (fidanacogene elaparvovec), its gene therapy for hemophilia B, ...
Roche is launching a new global phase 3 trial for the controversial Duchenne muscular dystrophy gene therapy Elevidys in ...
Morning Overview on MSN
First human trial tests gene therapy aimed at reversing cellular aging
For the roughly 80 million people worldwide living with glaucoma, daily life often means watching the world slowly close in.
Detroit patients getting HEMGENIX report life‑changing results; trial data show 94% off prophylaxis at five years.
The FDA’s recently unveiled plausible mechanism framework may have been forged with i | The FDA’s newly launched plausible ...
Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...
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