VANCOUVER — Autologous hematopoietic stem cell (HSC) gene therapy may offer a safe and effective alternative to allogeneic bone marrow transplant for patients with cerebral adrenoleukodystrophy, ...
NeuroVia Closes Series A Financing Round of $14M to Develop Novel Treatment Option for X-ALD Disease
CAMBRIDGE, Mass.--(BUSINESS WIRE)--NeuroVia, Inc., a biopharmaceutical company focused on developing innovative therapies for rare genetic neurological diseases, announced the closing of a Series A ...
Advanced liver disease (ALD) occurs when significant scarring causes the liver to lose function. Patients with ALD often have ...
Adrenoleukodystrophy (ALD) is rare X-linked genetic disease that affects the adrenal glands (found on top of the kidneys) as well as the myelin in the brain and spinal cord. The incidence of ALD is ...
Susan-Elizabeth Littlefield loves sharing the good news. She hosts a show on Sunday mornings based on local "positivity and empowerment," leading right into CBS Sunday Morning. MINNEAPOLIS – There has ...
Please provide your email address to receive an email when new articles are posted on . After screening, excessive drinking decreased from 46% to 32% at 6 months among those at risk for ALD. After 6 ...
SOMERVILLE, Mass.--(BUSINESS WIRE)--bluebird bio, Inc. (Nasdaq: BLUE) today announced the outcome of the U.S. Food and Drug Administration’s (FDA) Cellular, Tissue, and Gene Therapies Advisory ...
A nationwide, population-based cohort study of patients with imaging-confirmed hepatic steatosis assessed the long-term risks associated with three distinct steatotic liver disease subtypes. Liver and ...
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