Siren Biotechnology, pioneers of Universal AAV Immuno-Gene Therapy for cancer, today announced that the U.S. Food and Drug ...

A central nervous system (CNS) tumor has prompted the FDA to place clinical holds on two Regenxbio gene therapies, including ...

The FDA suspends Regenxbio gene therapy trials for Hurler and Hunter syndromes over safety concerns after a participant ...

Administration in the mid-to-high dose cohorts of the gene therapy trial will pause pending further evaluation.

A five-year-old patient dosed with RGX-111 has developed a brain tumour four years after being dosed with the gene therapy.

SpliceBio, a clinical-stage genetic medicines company pioneering protein splicing to address diseases caused by mutations in large genes, today announced that the first patient has been dosed in the ...

LONDON and NEW YORK, June 22, 2023 (GLOBE NEWSWIRE) -- MeiraGTx Holdings plc (NASDAQ: MGTX), a vertically integrated, clinical stage gene therapy company, today announced it will host a conference ...

Hubble Therapeutics selected Andelyn Biosciences, a CDMO, to manufacture adeno-associated virus (AAV) using its suspension AAV Curator™ platform to manufacture clinical grade AAV for the treatment of ...

(RTTNews) - MeiraGTx Holdings plc (MGTX), a vertically integrated, clinical-stage genetic medicines company, announced Tuesday positive top-line data from MGT-GAD-025, its clinical bridging study of ...

Creative Biolabs is helping researchers overcome challenges of gene therapy research by providing analytical testing ...

Genethon, a worldwide pioneer and leader in research and development of gene therapy for rare genetic diseases, and Hansa Biopharma, a Sweden-based leader in IgG cleaving enzyme technology announced ...